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Limb-Girdle Muscular Dystrophy (LGMD) - Diseases
*/ What is limb-girdle muscular dystrophy?Limb-girdle muscular dystrophy (LGMD) is a diverse group of disorders with many subtypes categorized by disease gene and inheritance. LGMD usually manifests in...
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Introducing New MDA National Ambassador Keisha Greaves and Checking in With...
Beginning in the early 1950s, when public awareness and understanding of muscular dystrophy and related neuromuscular diseases were extremely limited, MDA began calling upon individuals living with...
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Spotting Neuromuscular Disease in Adults
Chris AnselmoAfter years of denial, it was the stairs to his second-floor college apartment that forced Chris Anselmo to finally face his limb-girdle muscular dystrophy (LGMD) in 2009. “I remember...
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2022 Clinical & Scientific Conference March 14 Highlights
The conference officially kicked off at 9:30am CT with opening remarks from MDA President and CEO, Dr. Donald Wood.Today was the first full day of sessions of MDA’s 2022 Clinical & Scientific...
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2022 Clinical & Scientific Conference: March 16 Highlights
Today is the last day of 2022 MDA’s Clinical & Scientific Conference. The theme for today is clinical trials in neuromuscular disease (NMD)!HighlightsBest poster winnersAt the Highlight Session at...
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Five Questions with LGMD Researcher Martin Childers
Martin Childers, PhD, DO, chief medical officer at Asklepios BioPharmaceutical Inc. in North Carolina, was awarded an MDA research grant totaling $192,500 over one year to perform pre-clinical studies...
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People May Not Accept Your Disability. You Don’t Have to Accept That.
Tomeca Goodwin, 46, lives with a form of limb-girdle muscular dystrophy (LGMD). Born in Cincinnati, where she still resides, Tomeca has had a long career in community health. She also owns and creates...
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Research Study Alert: LGMD2I Natural History Study
Researchers at ML Bio Solutions are seeking individuals living with limb-girdle muscular dystrophy type 2I (LGMD2I, LGMD R9-FKRP-related) to participate in a 12-month natural history study. The...
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Clinical Trial Alert: LGMD2I Participants Sought for a Phase 3 Study
Researchers at PTC Therapeutics are looking for individuals with limb-girdle muscular dystrophy type 2I (LGMD2I) to participate in a phase 3 study. The goal of the study is to evaluate the efficacy of...
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Five Questions with LGMD Researcher Martin Childers
Martin Childers, PhD, DO, chief medical officer at Asklepios BioPharmaceutical Inc. in North Carolina, was awarded an MDA research grant totaling $192,500 over one year to perform pre-clinical studies...
View ArticleClik here to view.
Clinical Trial Alert: LGMD2I Participants Sought for a Phase 3 Study
Researchers at PTC Therapeutics are looking for individuals with limb-girdle muscular dystrophy type 2I (LGMD2I) to participate in a phase 3 study. The goal of the study is to evaluate the efficacy of...
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Research Study Alert: Researchers at Virginia Commonwealth University Seek...
Researchers at Virginia Commonwealth University are seeking participants living with limb-girdle muscular dystrophy type 2I (LGMD2I) to participate in a natural history study. This study aims to better...
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Introducing New MDA National Ambassador Keisha Greaves and Checking in With...
Beginning in the early 1950s, when public awareness and understanding of muscular dystrophy and related neuromuscular diseases were extremely limited, MDA began calling upon individuals living with...
View ArticleClik here to view.
2022 Clinical & Scientific Conference: March 16 Highlights
Today is the last day of 2022 MDA’s Clinical & Scientific Conference. The theme for today is clinical trials in neuromuscular disease (NMD)!HighlightsBest poster winnersAt the Highlight Session at...
View ArticleClik here to view.
2022 Clinical & Scientific Conference March 14 Highlights
The conference officially kicked off at 9:30am CT with opening remarks from MDA President and CEO, Dr. Donald Wood.Today was the first full day of sessions of MDA’s 2022 Clinical & Scientific...
View ArticleClik here to view.
MDA Partners with the Broad Institute on Rare Genomes Project for Limb-Girdle...
The Muscular Dystrophy Association (MDA) is pleased to announce a collaboration with the Broad Institute of MIT and Harvard, which aims to bring genetic diagnoses to more individuals living with...
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2019 MDA Engage LGMD Symposium Scheduled in Richmond on May 18
At MDA, we believe in the power of research and the importance of building relationships among families, clinicians, and the scientists making discoveries to advance treatments and therapies. We invite...
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Sarepta Therapeutics Announces Positive Results from the SRP-9003 Gene...
On June 8, Sarepta Therapeutics announced positive results from its first study in human patients of SRP-9003, a gene therapy designed to treat limb-girdle muscular dystrophy (LGMD) type 2E. Data from...
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Hacking COVID: MDA Staff Edition
In April, MDA fielded a survey to ask its community how COVID-19 was impacting their lives. We heard your responses — anxiety, questions, hope — and wanted to know more. In this six-part blog series,...
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How MDA is Supporting LGMD Research and Care in 2020
On July 18, MDA is hosting a free virtual Engage Limb-Girdle Muscular Dystrophy Symposium, a half-day educational event featuring key experts who will speak on topics including the latest in genetics...
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